A Boston Children’s Hospital trial of a repurposed experimental cancer drug has given parents, physicians, and scientists their first tantalizing evidence that it is possible to affect the course of a rare, fatal disease that causes children to age prematurely and die as teenagers. The disease, called progeria, affects only about 250 children worldwide, but is known to every medical student because of its heartbreaking trajectory and striking visual presentation, with children that almost seem to shrink into old age.
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